VIJAYAWADA: Founded by Sobharani Sunkara in 2019, the Amaravathi Rare Diseases Organisation (ARDO) has emerged as a beacon of hope for individuals suffering from muscular dystrophy (MD) in the State.
The Emirates Drug Establishment (EDE) has announced the approval of Itvisma (onasemnogene abeparvovec), a gene therapy that uses an adeno-associated viral vector to treat spinal muscular atrophy (SMA) ...