All muscular dystrophies cause muscle weakness, but life expectancy can vary dramatically between types of muscular dystrophy.

Sarepta reports positive, statistically significant results in a study evaluating the efficacy of its blockbuster gene ...

Muscular dystrophy is a disease caused by mutations in the dystrophin gene. The muscles of muscular dystrophy patients weaken and atrophy over time. Heart and breathing muscles may also eventually be ...

The family of a boy with a severe degenerative muscle disease has urged their local hospital to prescribe a drug that could help slow down the progress of the condition. Six-year-old Jack was ...

12-year-old Deklan Locke, who has Duchenne muscular dystrophy, uses a power wheelchair and raises awareness about the disease. Duchenne muscular dystrophy is a rare genetic disorder that causes muscle ...

New Evrysdi five-year data from the SUNFISH study showed continued stabilisation of motor function in a broad population of individuals with Types 2 or 3 spinal muscular atrophy (SMA) Late-breaking ...

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...