Precision DNA editing gene therapy achieves deep remissions in aggressive leukemia previously considered incurable.

Few companies stand better poised than Beam Therapeutics to reap the first fruits of the FDA’s promised flexibility toward cell and gene therapies. | Riding a regulatory win for its base editing ...

Modern medicine is one step closer to potentially curing sickle cell disease. On the heels of the U.K.'s authorizing the world’s first gene-edited treatment for sickle cell disease on Nov. 16, the U.S ...

Sickle cell disease (SCD) is a group of blood disorders, including sickle cell anaemia, that is caused by stem blood cells producing mutated red blood cells. This leads to health complications, as the ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

At age 45, Dr. Lakiea Bailey said, for the longest time, that she was the oldest person with sickle cell anemia that she knew. The executive director of the nonprofit patient advocacy group the Sickle ...

As people grow older, their immune systems do not simply slow down, they often become locked into a simmering, self-perpetuating state of inflammation. Emerging work now suggests that aging immune ...